Where Fabry disease is treated

NHS specialist centres in the UK

Fabry disease is rare enough that care is deliberately centralised. Diagnosis, enzyme replacement therapy and specialist monitoring are commissioned through a small number of designated lysosomal storage disorder (LSD) centres, rather than at every local hospital.

Always confirm current details before travelling. Centre names, contact details and referral routes can change. Your GP, local metabolic team, or the MPS Society can confirm the most current list and help arrange a referral. This page is a general guide, not a booking service.

England — adult centres

NHS England commissions Fabry disease diagnosis and treatment through five highly specialised adult centres.

Royal Free London — Lysosomal Storage Disorders Unit

London

Royal Free Hospital, Pond Street, London NW3 2QG

DiagnosisERT & oral therapyMultidisciplinary clinics

National Hospital for Neurology & Neurosurgery (UCLH) — Charles Dent Metabolic Unit

London

Queen Square, London WC1N 3BG

DiagnosisERT & oral therapyNeurology-linked care

Salford Royal Hospital

Manchester

Stott Lane, Salford M6 8HD

DiagnosisERT & oral therapyJoint adult/paediatric clinics

Queen Elizabeth Hospital Birmingham

Birmingham

Mindelsohn Way, Edgbaston, Birmingham B15 2GW

DiagnosisERT & oral therapy

Cambridge University Hospitals — Lysosomal Disorders Unit

Cambridge

Addenbrooke's Hospital, Hills Road, Cambridge CB2 0QQ

DiagnosisERT & oral therapy

England — paediatric centres

Three nationally commissioned centres manage children with lysosomal storage disorders, working closely with adult centres for transition to adult care.

Great Ormond Street Hospital — Metabolic Medicine

London

Great Ormond Street, London WC1N 3JH

Royal Manchester Children's Hospital — Willink Metabolic Unit

Manchester

Oxford Road, Manchester M13 9WL

Birmingham Women's & Children's Hospital — Metabolic Medicine

Birmingham

Steelhouse Lane, Birmingham B4 6NH

Scotland, Northern Ireland & Wales

Scotland

Inherited Metabolic Disorders in Scotland (IMD Scotland) is the managed clinical network that coordinates care for inherited metabolic disorders, including Fabry disease, across NHS Scotland. Its service is based at the Queen Elizabeth University Hospital & Royal Hospital for Children campus in Glasgow (NHS Greater Glasgow and Clyde), working with local health boards for day-to-day and shared care.

Northern Ireland

Belfast City Hospital provides paediatric and adult metabolic services, including care for Fabry disease, sometimes working jointly with English centres for specific aspects of treatment.

Wales

Similarly, patients in Wales are usually referred into an English centre for specialist LSD care, often alongside a local hospital for shared monitoring and infusions closer to home.

Cross-border referral arrangements can change — your GP or local health board can confirm the current pathway, and the MPS Society's advice line can help you understand what to expect.

How referral works

  • 1. Suspicion or family diagnosis

    A GP, another specialist, or a family diagnosis prompts consideration of Fabry disease — sometimes after years of unexplained symptoms such as pain, kidney or heart findings.

  • 2. Referral to a specialist centre

    Your GP or hospital consultant refers you to one of the centres above for enzyme and/or genetic testing. You don't need to live near a centre to be referred there — these services see patients from across the UK.

  • 3. Diagnosis & baseline assessment

    If confirmed, the specialist team carries out baseline assessments of the kidneys, heart and nervous system to understand how the condition is affecting you.

  • 4. Ongoing care

    Many people are monitored regularly at the specialist centre, with treatment (if needed) often able to move to a local hospital or homecare once established, in coordination with the specialist team.